CSG to Conduct KRX-101 Phase II/III Clinical Program
06 August 2003 - 12:18AM
UK Regulatory
The Collaborative Study Group to Conduct US-Based Phase II/III Clinical
Program for KRX-101 (sulodexide)for the Treatment of Diabetic Nephropathy
Study places KRX-101 in the hands of Clinical Leaders
In the field of Diabetic Nephropathy
NEW YORK, Aug. 5 -- Keryx Biopharmaceuticals, Inc.
(Nasdaq: KERX) announced today that the Collaborative Study Group (CSG), the
largest standing renal clinical trial group comprised of academic and tertiary
nephrology care centers, will conduct Keryx's US-based Phase II/III clinical
program for KRX-101 (sulodexide) for the treatment of diabetic nephropathy.
It is anticipated that the KRX-101 clinical program will commence by the late
third quarter or early fourth quarter of 2003.
KRX-101 is a first-in-class oral heparinoid compound that has been studied
extensively in Europe and is currently being marketed in select European,
Asian and South American markets by the Company's licensor for certain
cardiovascular indications. More than 20 studies have been published in
leading medical journals assessing the safety and efficacy of KRX-101 in
diabetic nephropathy and other vascular indications. Most recently, KRX-101
demonstrated significant efficacy in treating diabetic nephropathy in a
randomized, placebo-controlled, 223-patient Phase II clinical trial (the DiNAS
Study). This study was published in the June 2002 issue of the Journal of the
American Society of Nephrology.
"We believe this is an important validation of the potential for KRX-
101," said Michael S. Weiss, Keryx's Chairman and CEO. "The CSG is highly
selective in the drug candidates that it works with and has an outstanding
track-record of conducting high quality, medically important clinical trials
in the field of renal care and diabetic nephropathy. In fact, each of their
last 3 major clinical trials led to product approvals, including the recent
approval of Bristol-Myers Squibb's and Sanofi's drug, irbesartan (Avapro(R)),
an angiotensin receptor blocker (ARB) for diabetic nephropathy." Mr. Weiss
continued, "We are very excited to place our Phase II/III clinical program for
KRX-101 in the hands of these leading renal care and diabetes specialists so
that it may finally begin to benefit the millions of patients that continue to
suffer from this disease."
Dr. Edmund J. Lewis, Principal Investigator of CSG commented, "KRX-101 is
an exciting and promising treatment for diabetic nephropathy. The positive
data from the DiNAS Phase II clinical trial is the culmination of over 20
years of research, which provides consistent pre-clinical and clinical
evidence for the benefits of this drug in this disease and related conditions.
Since the mechanism of action appears to be completely independent of the
angiotensin system, the target of current interventions in this area, this
compound represents a truly novel approach to treating the disease. We are
genuinely excited for our patients about the prospects of this new agent. "
Dr. Lawrence Hunsicker, Co-Chairman of CSG added "We are enthusiastic
about working with Keryx on the development of KRX-101. Data generated to
date indicates that KRX-101 may offer significant benefit above and beyond
that which we are currently able to achieve with ACE inhibitors and ARBs, the
current first-line of therapy for this disease. This is extremely important
since despite these existing therapies, the number of patients progressing to
end stage renal disease continues to climb at an alarming rate. We are
looking forward to commencing this important clinical program as soon as
possible."
ABOUT THE COLLABORATIVE STUDY GROUP
The Collaborative Study Group (CSG), the largest standing renal clinical
trials group, is comprised of academic and tertiary care physician-researchers
interested in collaborative clinical trials investigating new therapeutic
approaches in the treatment of kidney disease. Since 1979 the CSG has
conducted multiple large-scale clinical trials resulting in over 40 major
publications in peer-reviewed journals. The CSG trial of ACE Inhibition in
Type 1 Diabetic Nephropathy and the recently completed trial of Irbesartan in
Type 2 Diabetic Nephropathy (I.D.N.T.) led to FDA product registration for new
indications and the recommendation of these agents as standard of care by the
American Diabetes Association. The results of each of the CSG's last 3 major
clinical trials were published in the New England Journal of Medicine. The
recently completed IDNT multi-national trial in collaboration with Bristol-
Myers Squibb and Sanofi-Synthelabo is the largest trial in renal disease to
date, consisting of 1,715 patients from 210 investigative sites worldwide.
ABOUT KRX-101
KRX-101 (sulodexide), a first-in-class oral heparinoid compound, is being
developed for the treatment of diabetic nephropathy, a progressive and life-
threatening kidney disease which afflicts approximately 3 million diabetics in
the United States alone.
KRX-101 belongs to a proposed new class of nephroprotective (kidney
protecting) drugs, called glycosaminoglycans. A variety of members of this
chemical family have been shown to decrease pathological albumin excretion in
diabetic nephropathy in man. However, these heparin agents all require
therapy by injection and are all potent anticoagulants, which are blood
thinners capable of inducing bleeding. Sulodexide, on the other hand, is
given orally and, in this form, has demonstrated little, if any, anticoagulant
effects to date.
More than 20 studies have been published in leading medical journals
assessing the safety and efficacy of KRX-101 in diabetic nephropathy and other
vascular conditions. Most recently, KRX-101 demonstrated significant efficacy
in treating diabetic nephropathy in a randomized, placebo-controlled, 223-
patient Phase II clinical trial (the DiNAS Study) conducted in Europe. In
this study, Type 1 and Type 2 diabetics with diabetic nephropathy were treated
daily for 4 months with 50, 100- and 200-milligram gelcaps of KRX-101 and
showed substantial dose-dependent reduction in proteinuria, with the highest
dose achieving a 74% reduction versus placebo following four months of
treatment. In addition, the data in the DiNAS Study showed that the
therapeutic effect of KRX-101 was additive to ACE-inhibitor treatment,
suggesting that KRX-101 operates under a different mechanism of action than do
ACE inhibitors and Angiotensin Receptor Blockers ("ARBs"), which represent the
existing first line of treatment for the disease. These findings were
published in the June 2002 issue of the Journal of American Society of
Nephrology.
KRX-101 (sulodexide) has a well-established safety profile based upon
nearly twenty years of marketing experience by the Company's licensor and use
by thousands of patients (representing over 50 million patient days of use) in
Italy, Spain, Eastern Europe, Asia, and South America as a cardiovascular
drug.
In 2001, KRX-101 was granted Fast-Track designation for the treatment of
diabetic nephropathy and, in 2002, the Company announced that the FDA had
agreed, in principle, to permit the Company to avail itself of the accelerated
approval process under subpart H.
ABOUT DIABETIC NEPHROPATHY
According to The American Diabetes Association, there are an estimated 16
million diabetics in the United States, of which 90%-95% are Type II
diabetics. Approximately 20% of all diabetics develop diabetic kidney disease,
a condition known as diabetic nephropathy. Therefore, it is estimated that
there are approximately 3 million people suffering from the disease in the
U.S. alone. Diabetes is now the most common cause of End Stage Renal Disease,
or ESRD, in the US and in many other developed nations, and represents 44% of
all new cases of ESRD in the US. Despite advances in clinical care, including
improvements in glycemic (blood sugar) control and blood pressure control, the
number of diabetes related cases of ESRD continues to rise. In particular, the
incidence of Type II diabetes-related ESRD is rapidly increasing. Less than
20% of diabetics on dialysis in the US survive for five years, making the
mortality of end-stage renal failure in this group higher than in most forms
of cancer. Unfortunately, renal transplantation is an option for less than 20%
of diabetics with end-stage renal disease (as compared to 40-50% of non-
diabetics), principally due to age and concomitant vascular disease. Thus,
despite recent advances, diabetic nephropathy remains a potentially
catastrophic illness for which partial, but insufficient treatment is
available today.
ABOUT KERYX BIOPHARMACEUTICALS, INC.
Keryx Biopharmaceuticals, Inc. (Nasdaq: KERX; London AIM: KRX) is a
biopharmaceuticals company focused on the acquisition, development and
commercialization of novel pharmaceutical products for the treatment of
serious, life-threatening diseases, including diabetes and cancer. Keryx is
developing KRX-101 (sulodexide), a novel first-in-class oral heparinoid
compound, for the treatment of diabetic nephropathy, for which Keryx is
currently planning its U.S.-based Phase II/III clinical program. Keryx also
has an active in-licensing program designed to identify and acquire clinical-
stage drug candidates. Additionally, Keryx is seeking partners for its
KinAce(TM) drug discovery technology and related products. Keryx
Biopharmaceuticals is headquartered in New York City.
Cautionary Statement
Statements contained or referenced in this news release that are not
historical facts, including, but not limited to, statements concerning Keryx's
ability to successfully begin and complete clinical trials of KRX-101, may be
forward-looking statements, as the term is defined in the Private Litigation
Reform Act of 1995. In some cases, you can identify forward-looking statements
by terminology such as "anticipate", "estimate", "expect", "project", "hope",
"should', "intend", "plan", "believe", "scheduled", will" and other words and
terms of similar meaning in connection with any discussion of future operating
or financial performance. Important factors may cause Keryx's actual results
to differ materially, including: adverse results in its clinical development
processes; failure to obtain patent protection for its discoveries; commercial
limitations imposed by patents owned or controlled by third parties;
difficulties or delays in obtaining regulatory approvals to market products
resulting from its development efforts; difficulties or delays in obtaining
clinical or commercial supplies of our product candidates; and the requirement
for substantial funding to conduct research and development, and to expand
commercialization activities. Important factors that might cause or contribute
to such a discrepancy include, but are not limited to, the risks discussed
under the heading "Risk Factors" in our Annual Report or Form 10-K, which has
been filed with the Securities and Exchange Commission, as well as other
filings we periodically make with the Commission. Any forward-looking
statements set forth in this news release speak only as of the date of this
news release. Keryx does not intend to update any of these forward-looking
statements to reflect events or circumstances that occur after the date
hereof. This press release and prior releases are available at www.keryx.com.
The information in Keryx's website is not incorporated by reference into this
press release and is included as an inactive textual reference only.
KERYX CONTACT:
Ron Bentsur
Vice President Finance and Investor Relations
Keryx Biopharmaceuticals, Inc.
Tel: +1-212-531-5965
E-mail: ron@keryx.com
SOURCE Keryx Biopharmaceuticals, Inc.
-0- 08/05/2003
/CONTACT: Ron Bentsur, Vice President Finance and Investor Relations of
Keryx Biopharmaceuticals, Inc., +1-212-531-5965, ron@keryx.com/
/Web site: http://www.keryx.com /
(KERX)
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